Educational | Azafaros B.V.

Patient Resources and Patient Organizations we collaborate with

We aim to keep these resources up-to-date to provide important information on supporting partners for patients, their families, and caregivers.

At Azafaros, we value highly the important work of patient-focused organizations and communities. Through close collaborations and partnerships, our goal is to understand patients’ needs, support the patient community, and maintain a close and regular dialogue with patient organizations. We are committed to applying these insights to our programs and activities.

Videos

With the help of patients, patient families, physicians, and partner companies, we have created several videos to encourage a better understanding of these diseases, our lead program nizubaglustat, and to provide information about our ongoing PRONTO study. Please click on the links below to watch these videos.

DISCLAIMER: Please note that these videos were created for a specific audience. They should be viewed by physicians or patient families who have expressed an interest in taking part in a future clinical trial organised by Azafaros.

Nizubaglustat Mode of Action

Treatment development for GM1 and GM2 gangliosidoses

This video has been created by Azafaros in close collaboration with the GM1 and GM2 community to provide information on how a potential treatment developed for GM1 and GM2 gangliosidosis may work. It aims to explain the diseases and educate patients and families on the possible mechanism and mode of action of Azafaros’ compound, nizubaglustat.

To select a suitable language, click the orange button to go to the original movie. There you can choose from English, German, Brazilian Portuguese or Spanish (Latin America).

Choose language

What is the PRONTO study?

PRONTO is a natural history study aiming to understand how GM1 and GM2 gangliosidoses progress over time, which might help researchers understand how the condition develops and possibly how to treat it in the future. In the short video below, you can learn more about what PRONTO is, and why it is important.

To select a suitable language, click the orange button to go to the original movie. There you can choose from English, German, Brazilian Portuguese or Spanish (Latin America).

Azafaros for Patients

Patient Resources and Patient Organizations we collaborate with

Videos

Nizubaglustat Mode of Action

What is the PRONTO study?

Patient Organizations we collaborate with

Patient organizations GM1 Gangliosidosis

Patient organizations GM2 Gangliosidosis

Niemann-Pick Associations