We are Azafaros

A beacon for people living with severe rare metabolic disorders.

A team of highly experienced industry experts

Azafaros is supported by a syndicate of leading Dutch and Swiss investors. Our clinical candidate AZ-3102 is an orally available azasugar designed to treat the central nervous system and to interfere with the metabolism of glycosphingolipids affecting key disease pathways through a unique dual mode of action.
Azafaros aims to be a beacon for patients living with severe rare genetic diseases and their families.

– Since 2018


Azafaros Announces FDA Grant of Orphan Drug Designation for AZ-3102 in the Treatment of Niemann-Pick Disease

Azafaros Presents Positive Clinical and Preclinical Data Supporting Development of Lead Compound AZ-3102 in Lysosomal Storage Disorders at the 18th Annual WORLDSymposiumâ„¢ Conference