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About Us
Our Story and Mission
Our Board of Directors
Our Leadership Team
Our Investors
Our Science
Lysosomal Storage Disorders
Our Lead Programme
Azafaros for Patients
Disease information
Our Therapeutic Approach
Patient Resources and Organizations
Expanded Access Policy
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Connect with Azafaros
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June 8, 2023
Azafaros Announces Enrollment of First Patient in Phase 2 RAINBOW Study Evaluating AZ-3102 in GM2 and NP-C Patients
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March 20, 2023
Azafaros Appoints Chief Operating Officer and Head of Finance
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February 27, 2023
Beyond Biotech podcast 35: Rare Disease Day
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February 20, 2023
Azafaros Receives Additional Regulatory Designations for AZ-3102 from FDA, EMA and MHRA
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January 9, 2023
Azafaros Strengthens Medical and Scientific Management Team Reflecting Clinical Progress
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January 5, 2023
BREAKING NEWS: Azafaros Receives FDA’s IND Clearance and Fast Track Designation
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April 24, 2022
Azafaros Announces FDA Grant of Orphan Drug Designation for AZ-3102 in the Treatment of Niemann-Pick Disease
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February 14, 2022
Azafaros Presents Positive Clinical and Preclinical Data Supporting Development of Lead Compound AZ-3102 in Lysosomal Storage Disorders at the 18th Annual WORLDSymposiumâ„¢ Conference
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February 1, 2022
Azafaros Receives FDA Orphan Drug Designation for AZ-3102 in GM2 Gangliosidosis
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January 18, 2022
Azafaros Announces Multiple Presentations at 18th Annual WORLDSymposiumâ„¢
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June 30, 2021
Azafaros Appoints Stefano Portolano, M.D., as Chief Executive Officer
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April 6, 2021
Azafaros enters clinical stage with AZ-3102, an oral small molecule being developed for rare neurogenetic disorderss
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June 10, 2020
Azafaros expands executive management team and operations
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February 6, 2020
Azafaros completes EUR 25 million Series A financing to advance rare metabolic disorders pipeline
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July 23, 2018
Azafaros B.V. secures seed funding to develop new treatments in rare metabolic disorders
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About Us
Our Story and Mission
Our Board of Directors
Our Leadership Team
Our Investors
Our Science
Lysosomal Storage Disorders
Our Lead Programme
Azafaros for Patients
Disease information
Our Therapeutic Approach
Patient Resources and Organizations
Expanded Access Policy
News
Events
Connect with Azafaros
Studies