AZ-3102 Mode of Action Treatment development for GM1 and GM2 gangliosidosis
This video has been created by Azafaros in close collaboration with the GM1 and GM2 community to provide information on how a potential treatment developed for GM1 and GM2 gangliosidosis may work. It aims to explain the diseases and educate patients and families on the possible mechanism and mode of action of Azafaros’ compound, AZ-3102.
To select a suitable language, click the orange button to go to the original movie. There you can choose from English, German, Brazilian Portuguese or Spanish (Latin America).
What is the PRONTO study?
PRONTO is a natural history study aiming to understand how GM1 and GM2 gangliosidoses progress over time, which might help researchers understand how the condition develops and possibly how to treat it in the future. In the short video below, you can learn more about what PRONTO is, and why it is important.